For over a year, PPMD has been working with Congress on landmark legislation called 21st Century Cures. The bill aims to speed the discovery, development, and delivery of therapies for diseases that have an unmet medical need like Duchenne. We have been thankful to Congress for their willingness to meaningfully engage the patient community in the process. This week the House will hold a floor vote on the measure (HR 6.) We need all House members to vote YES to get this bill over the finish line in the House of Representatives.

Please take one minute to send your House member an Action Alert telling them to vote YES on HR 6, the 21 Century Cures Act.

This bill contains provisions that will:

• Increase funding for the National Institutes of Health (NIH) & the Food & Drug Administration (FDA)
• Incorporate the patient perspective into the drug development and regulatory review process (patient focused drug development)
• Clarify the use of platform technologies - Utilizing early data from trials to shorten follow on trials (such as in exon skipping)
• Provide new incentives for the development of drugs for rare diseases (OPEN Act)
• Invest in 21st century science and next generation investigators

We are nearly there with this important legislation, and with your help the House will make this promise of a new day in drug discovery a reality. Then it will be on to the Senate...