On Thursday, September 28, an FDA Advisory Committee will review ataluren for potential approval and use within our Duchenne community.
The Duchenne community is joining forces in a show of strength to…
Added by PPMD on September 27, 2017 at 6:42pm — No Comments
PPMD is excited to announce that we will continue a grant program to help support our Certified Duchenne Care Center (CDCC) Program. The CDCC Program is a network of…
Added by PPMD on September 27, 2017 at 12:30pm — No Comments
This weekend, nearly every televised College Football game around the country will have coaches wearing Coach To Cure MD armbands, tweeting about Duchenne, and encouraging fans to text a…Continue
Added by PPMD on September 26, 2017 at 1:00pm — No Comments
Added by PPMD on September 26, 2017 at 9:30am — No Comments
Santhera Pharmaceuticals announced that the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a negative opinion for its Type II extension application for Raxone® (idebenone) in Duchenne. Santhera plans to appeal the opinion and will seek a re-examination by the CHMP. We appreciate…Continue
Added by PPMD on September 15, 2017 at 8:00am — No Comments
Today Parent Project Muscular Dystrophy (PPMD) named Nemours/Alfred I duPont Hospital for Children (Nemours) in Wilmington, Delaware our 17th Certified Duchenne Care Center.
PPMD’s Certified Duchenne Care Center Program, which supports standardized, comprehensive care and services for all…Continue
Added by PPMD on September 14, 2017 at 8:30pm — No Comments
The deadline to submit a written comment for the FDA Advisory Committee Meeting on ataluren is this upcoming Thursday, September 14th.
To make a comment,…Continue
Added by PPMD on September 12, 2017 at 9:30am — No Comments
PPMD is excited to announce next year’s lineup of areas we will visit as part of our End Duchenne Tour!
Combining each of the pillars that make up PPMD’s mission, the End Duchenne Tour brings updates on research, advocacy, and care to cities across the country, featuring a roster of leading experts in the…
Added by PPMD on September 8, 2017 at 5:30pm — No Comments
Added by PPMD on September 6, 2017 at 10:00am — No Comments
Earlier this year, Bristol-Myers Squibb (BMS) announced it had entered into an agreement to license BMS-986089 (RG6206), an anti-myostatin adnectin in development for Duchenne muscular dystrophy, to Roche. Today, the Roche team has provided an update to our…Continue
Added by PPMD on September 5, 2017 at 9:30am — No Comments