Join us September 24th as thousands of coaches from hundreds of universities wear the Coach To Cure MD patch on their sleeve to raise awareness. Families will join teams on the field on game day and will share their stories with spectators and media. We also…

Today, PPMD sent a letter to the FDA requesting updates on various regulatory actions of tremendous importance to the Duchenne community. In our letter, we are asking the FDA to talk to our community, tell us what is going on, and confirm that…

Marathon Pharmaceuticals announced this morning that the U.S. Food and Drug Administration (FDA) has accepted Marathon’s New Drug Applications (NDAs) for the investigational drug deflazacort for Priority Review. The NDAs are for an immediate-release tablet formulation and an oral suspension formulation of deflazacort for the…

Today, Summit Therapeutics plc announced positive results from a Phase 1 trial of a new formulation of…

The 9th Annual Coach To Cure MD on September 24 is shaping up to be the biggest year yet!

Duchenne mom Kim Powers shares why this is the year you should get in the game and help us #TackleDuchenne:…