The FDA has notified Sarepta that they are continuing their review of eteplirsen and will not be able to complete their work by the Prescription Drug User Fee Act (PDUFA) goal date of May 26, 2016.…Continue
Added by PPMD on May 25, 2016 at 12:00pm — No Comments
PPMD Awards Eleventh Clinic Certification as Part of Effort to Ensure People with Duchenne Receive Optimal Care
Children’s Mercy Hospital (Children’s Mercy) in Kansas City, Missouri, became the 11th clinic named…Continue
Added by PPMD on May 16, 2016 at 2:08pm — No Comments
For more than two years, PPMD has been leading a national effort to build a newborn screening infrastructure for Duchenne in the U.S.
Led by PPMD's Annie Kennedy, Michele Lloyd–Puryear, M.D., Ph.D., Newborn Screening Consultant for PPMD, and Jerry Mendell, MD of Nationwide Children's, the effort includes more than 50 of the worlds top newborn screening…Continue
Added by PPMD on May 16, 2016 at 8:30am — No Comments