On Monday, April 25, an FDA Advisory Committee will review eteplirsen for potential approval and use within our Duchenne community.
The Duchenne community is joining forces in a show of strength to demonstrate to the FDA our community’s support for our robust therapeutic pipeline. Over 850 Duchenne community members are scheduled to attend the…
ContinueAdded by PPMD on April 21, 2016 at 8:30am — No Comments
The briefing documents for Sarepta’s Ad Comm on Monday, April 25th have been released. Like you, we will spend the next several days dissecting these documents so…
ContinueAdded by PPMD on April 21, 2016 at 8:00am — No Comments
All your calls, emails, and Hill visits during our February Advocacy Conference (in the pouring rain!) are yielding GROUND BREAKING RESULTS.
Yesterday, the Federal Appropriations Report Language for…
ContinueAdded by PPMD on April 19, 2016 at 4:00pm — No Comments
PPMD Awards Tenth Clinic Certification as Part of Effort to Ensure People with Duchenne Receive Optimal Care
Children’s Hospital Los Angeles (CHLA) became the tenth clinic named a Certified Duchenne Care Center by Parent Project Muscular Dystrophy (PPMD). PPMD’s Certified Duchenne…
ContinueAdded by PPMD on April 19, 2016 at 9:00am — No Comments
PPMD will host our 22nd Annual Connect Conference in Orlando, June 26-29. This will be an incredible coming together of the community's most…
ContinueAdded by PPMD on April 15, 2016 at 10:30am — No Comments
Added by PPMD on April 14, 2016 at 2:26pm — No Comments
Late in 2015, Parent Project Muscular Dystrophy (PPMD) and our research partners at Johns Hopkins Bloomberg School of Public Health (JHSPH) released the results of our second patient-centered…
ContinueAdded by PPMD on April 13, 2016 at 4:00pm — No Comments
Catabasis announced positive biomarker data from Part A of the MoveDMD trial, as well as initiation of dosing for the first patient for Part B (Phase 2) - a 12-week trial to assess the efficacy of CAT-1004 in Duchenne. We look forward to continued success from our partners at…
ContinueAdded by PPMD on April 12, 2016 at 9:30am — No Comments
PPMD is excited to unveil the agenda for the 22nd Annual Connect Conference in Orlando, June 26-29 at… |
Added by PPMD on April 11, 2016 at 1:16pm — No Comments
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