It is exactly what we were hoping for. Exactly what we dreamed about long ago. Big Pharma in the form of GSK has made a deal with Prosensa. PPMD and many other organizations have provided seed funding… funding in small bits to grow the work at each step along the way with the understanding that success would attract money and partnerships. The strategy worked!
Today is monumental for Duchenne.
Some months ago, I presented at BIO. Rare Disease was a focus of one of the… Continue