Featured Blog Posts – January 2015 Archive (7)

Parent Project Muscular Dystrophy Awards UCLA $50,000 Exploratory Grant for Evaluation of Exon Skipping Enhancers in Duchenne

PPMD announced today that they will award Dr. M. Carrie Miceli and her team at UCLA’s David Geffen School of Medicine and College of Letters and Science, a $50,000 exploratory grant to continue their evaluation of exon skipping boosters for the treatment of Duchenne. 


Duchenne muscular dystrophy is the most common fatal genetic disorder diagnosed in…


Added by PPMD on January 29, 2015 at 1:00pm — 2 Comments

Get Active in Advocacy

2014 was a historic year in our community. 2015 promises to be another critical year in Duchenne and we need you to help keep the momentum going! Just look at the ‘to-do’ list:

  • MD-Care Act amendment implementation begins
  • New Drug Applications submissions expected by several companies
  • The FDA has stated publicly…

Added by Ryan Fischer on January 28, 2015 at 1:30pm — No Comments

Important Vaccinations Recommendations

Vaccinations are very, very important to protect us against infection and disease – but they are also very, very confusing. 

Some vaccines are “live,” some are “attenuated (killed),” some protect against viral infections, some protect against bacterial infections, some are…


Added by Kathi Kinnett on January 23, 2015 at 12:00pm — No Comments

BMS & The Voice of the Patient

For the last two years, global biopharmaceutical company Bristol-Myers Squibb (BMS) has organized a day when all of their drug development project teams from across the world would have the opportunity to take some time to listen to patients and their caregivers. Wednesday was that…


Added by Pat Furlong on January 22, 2015 at 10:30am — 1 Comment

Meet our 2015 PPMD Adult Advisory Council!

“We were the generation that was hoped for… And now we’re here.” L. Vance Taylor

The PPMD Adult Advisory Council (PAAC) serves to ensure that the voices of adults living with Duchenne and Becker muscular dystrophy are reflected in…


Added by Annie Kennedy on January 15, 2015 at 1:00pm — No Comments

Where the Long, Winding Path has Led

I sit here in my home office on a snowy January day in Maryland, and I think about where I am at now in life and how I got here. As a naïve, newly minted Ph.D. in 1980, it wasn’t inevitable, or even predictable, that I would ultimately join all of you in the fight to end Duchenne. But, I’m really glad that I’m here and I’ll tell you a bit about the path along…


Added by John D. Porter, PhD on January 12, 2015 at 10:00am — 1 Comment

Update on the 2015 Flu

As you may have noticed, despite receiving the 2014-2015 influenza (flu) vaccine, many people have gotten the flu.  It turns out that the vaccine contained inactivated (dead) virus that protected against 3 strains of influenza:


  • Influenza B/Massachusetts (2012-like antigen)
  • Influenza A/California (H1N1 – like…

Added by Kathi Kinnett on January 9, 2015 at 10:28am — 6 Comments

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