We are pleased to report our final numbers for the FY19 letters.
In total, 19 Senators signed onto the Senate FY19 letter, joining 51 members of the House. That makes a solid 70 members of Congress (House and Senate combined) sending a strong message of support behind Duchenne research, public health, drug development, and patient support initiatives. They provide strategic direction for the federal agencies that touch Duchenne. Given the…Continue
Patient-Focused Drug Development in action
Companies developing gene therapies, the FDA, and other stakeholders are interested in the treatment priorities of the Duchenne community. Because of this, PPMD has collaborated with RTI International, with financial support from Solid Biosciences and…
The PPMD Advocacy Conference registration is live! Join us March 4-6 in Washington DC to advocate for Duchenne directly with Members of Congress.