Today – the Better Empowerment Now to Enhance Framework and Improve Treatments (BENEFIT) Act, S. 1052 – led by Sen. Roger Wicker (R-MS) and Sen. Amy Klobuchar (D-MN) passed in the Senate!
This means that – thanks to the leadership of our Senate champions and our Duchenne community – the agency’s signature tool for evaluating risk-benefit may soon have to include data from the patient perspect…