Exon skipping 53

19 members Latest Activity: Jun 16, 2018

Hi,

My son has deletion 48-52 and need 53 skipped. Want to get in touch with any one who needs 53 skipped.

Thanks,

Amrit

ataluren trial following up

13 members Latest Activity: May 13, 2016 discussion about what we have to do

Mom's Cafe

124 members Latest Activity: Oct 8, 2020 A group for Mom's who like to vent and talk about life with DMD kids

Older men with Duchenne's (18 +)

10 members Latest Activity: Aug 20, 2013

For older men affected with DMD, and people living with older guys, its not just the parents living with DMD. This is a place for us older guys…

Premature Stop Codon

76 members Latest Activity: Jul 5, 2016

Duchenne Smiles

115 members Latest Activity: Feb 27, 2014 A Duchenne smile is a True smile, cannot be faked and exemplifies true enjoyment.

Teenagers (age 13-18)

66 members Latest Activity: Jun 24, 2020

New York Families

44 members Latest Activity: Feb 18, 2015

Discussion group for families in New York on fundraising events, care, advocacy.

Cincinnati Children's Hospital Medical Center

193 members Latest Activity: Sep 17, 2015

For families who take their children to Cincinnati Children's Hospital for DMD/BMD  medical care.