PTC 124-2b Clinical Trial


PTC 124-2b Clinical Trial

Various issues re: PTC 124 Clinical Trials for current or prospective participants worldwide

Members: 31
Latest Activity: May 1, 2018


PTC124 now has a name...

Started by Paul Johnson. Last reply by Paul Johnson Feb 3, 2009. 1 Reply

PTC124 in the courts

Started by Paul Johnson. Last reply by Paul Johnson Dec 22, 2008. 4 Replies

Is the 2b Trial Full?

Started by Paul Johnson. Last reply by brad stringer Dec 4, 2008. 1 Reply

Comment Wall


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Comment by Marks33 on September 3, 2011 at 7:15am
Please see

Obviously need to find out what the implications are for the planned trial outside N America
Comment by Blazena Kaderabkova on September 1, 2011 at 5:38pm

Have a look that the study is prolonged 10/2012

Comment by Chad Studebaker on September 1, 2011 at 4:20pm
They have just extended the 36 weeks until FDA approval can be it seems this trial phase is at a holding point.  I am not sure this is a function of PTC.  Perhaps this is more about FDA taking more time to review the data and applications for orphan drug status.
Comment by Perlita & Gordy Hains on September 1, 2011 at 10:51am

I haven't heard much either - heading to CHOP mid sept, hopefully they can shed some light - I keep in close contact w/ Jill Castle from AZ... her son was & is on the trial - maybe she can shed some light.   xoxo from PA


Comment by Gregoris Panayiotou on September 1, 2011 at 10:15am

Yeah,  What is going on with Ataluren? Do we have any news from PTC?

This shows how all these drugs would take decades to be marketed.  And it seams that PTC is not as orginised and willing to go on.

I am very dissapointed with PTC's management of this trials and progress.



Comment by Dinuka Pramod Samarakoon on September 1, 2011 at 9:33am
I am from sri lanka living with duchenne is not easy here,i am the only child in my family
Comment by Donna on September 1, 2011 at 9:24am
Really don't have much of an update.  My son is on it.  We go for doc visits every 12 weeks just for blood work really is all.  I don't know the status of the drug itself. 
Comment by Dinuka Pramod Samarakoon on September 1, 2011 at 9:23am
is there anyone who can take me to the trial,,,,,,,,,
Comment by Clare Harper on September 1, 2011 at 6:14am
is anyone able to chime in on  how things are progressing now with phase 3?
Comment by Stegmann Sacha on March 4, 2010 at 3:01pm
After the PTC press release ( the way will be more difficult now... sorry for our hopeful boys!

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