My 7 year old son, Evan was diagnosed with Duchenne this past May. He has the deletion of exon 44. We would need a skip of exon 43 or 45.
It looks like Sarepta and Prosensa have pre-clinical trials for skipping exon 45 but doesn't seem that they have not been moving forward with it. Does anyone know if they are waiting to see the outcome of exon 51? Or know where I can find out more details?
If exon 51 gets approval will it be a faster process for the others?