Please sign this petition to show your support and to urge PTC Therapeutics to provide a new Open Study for ALL children with nonsense mutation using the drug PTC 124.
Thanks for posting the petition. The word just came down that Jacob is denied the drug. I thought PTC Pharmaceuticals wanted to help all the families. I don't understand this. I really don't understand.
I start this petition with the help of Berit. I think that we need much signs to show any force. If we have much and much signs we can present this petition to research community and companies to demonstrate that we don't agree with the actual course of research. I want to show this petiton in a World Muscle meeting if the petition have significance.In 2006 I post in my website the top ten of Advances in Pharmacological Approach in DMD. After 2006 I don't see nothing to include in any top ten for this generation. Anybody can give me any news for treat our sons now?