for that reason we have to be open to other researchs for example the utrophin I think that is in the body of all of our kids it has to be activated I might be wrong. The thing is to find a solution for all our kids and not to loose hope
Hopefully (prayers and fingers crossed), UTROPHIN and ACE-031 will work for all our kids. May be together they can work as a CURE also. We all are waiting for results of BMN-195. They said, we should hear someting in Q3 2010. There is conf call by Biomarin on 2nd AUG. Hopefully, they will say something postive about BMN-195 in that call.
BioMarin just announced their utrophin didn't work in their Phase I clinical trial. Looks like this will fall off the menu for quite some time. :(
It is a setback, but they did say that they have a new candidate compound that overcomes the limitations of BMN 195. Its just a question of whether they do continue with this and how long it will take to get into trials.
cheryl cliff said: