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the response was not really clear, if you message me your email i will forward it to you if you'd like
Ofelia Marin said:Does he give an explanation of why he thinks exon skipping will not become an effective treatment (if approved)? What does he think would be a better alternative?
jenn said:i know dr brian at mass general in boston seemed to not like exon skipping at all when i asked him if that hospital may be a site for avi or prosensa... so confusing for sure!
Laurie Paschal said:I'm confused, too. We were there in August and she didn't say a word to us.
jenn said:im confused, we are also dr wongs patients, and also set to hopefully take part in the trial at nationwide childrens...but dr wong never told us about her possible trial, in fact i believe she mentioned we would have choices, prosensa or avi, in the next year but no further info. if anyone has info on where prosensa will be doing their trials id love to hear it.
Who thinks exon skipping will NOT an effective treatment?
jenn said:the response was not really clear, if you message me your email i will forward it to you if you'd like
Ofelia Marin said:Does he give an explanation of why he thinks exon skipping will not become an effective treatment (if approved)? What does he think would be a better alternative?
jenn said:i know dr brian at mass general in boston seemed to not like exon skipping at all when i asked him if that hospital may be a site for avi or prosensa... so confusing for sure!
Laurie Paschal said:I'm confused, too. We were there in August and she didn't say a word to us.
jenn said:im confused, we are also dr wongs patients, and also set to hopefully take part in the trial at nationwide childrens...but dr wong never told us about her possible trial, in fact i believe she mentioned we would have choices, prosensa or avi, in the next year but no further info. if anyone has info on where prosensa will be doing their trials id love to hear it.
This just in from Dr. Wong.... again too hard to wait. First come first serve.... Looks like if Nicolas is able to be a part of AVI, we wil be there...
"Per Prosensa, the PRO051 trials will be conducted by GSK - timeline - JULY, AUGUST OR September 2010"
So "early" 2010, as Prosensa stated couple of months ago, is now July, August or September 2010... Looks like the fact that GSK is planning the trials will postpone the start (?).
Wouldn't it be great if we could do the same with our boy's DMD progression, stop it for 6 months or so? For them 6 months delay might not seem like a big deal but for us it is.
Michelle Gonzales said:This just in from Dr. Wong.... again too hard to wait. First come first serve.... Looks like if Nicolas is able to be a part of AVI, we wil be there...
"Per Prosensa, the PRO051 trials will be conducted by GSK - timeline - JULY, AUGUST OR September 2010"
So "early" 2010, as Prosensa stated couple of months ago, is now July, August or September 2010... Looks like the fact that GSK is planning the trials will postpone the start (?).
Wouldn't it be great if we could do the same with our boy's DMD progression, stop it for 6 months or so? For them 6 months delay might not seem like a big deal but for us it is.
Michelle Gonzales said:This just in from Dr. Wong.... again too hard to wait. First come first serve.... Looks like if Nicolas is able to be a part of AVI, we wil be there...
"Per Prosensa, the PRO051 trials will be conducted by GSK - timeline - JULY, AUGUST OR September 2010"
Ofelia:
High five on that comment. I'll take stopping the disease for six months - no problems!!!!
Ofelia Marin said:So "early" 2010, as Prosensa stated couple of months ago, is now July, August or September 2010... Looks like the fact that GSK is planning the trials will postpone the start (?).
Wouldn't it be great if we could do the same with our boy's DMD progression, stop it for 6 months or so? For them 6 months delay might not seem like a big deal but for us it is.
Michelle Gonzales said:This just in from Dr. Wong.... again too hard to wait. First come first serve.... Looks like if Nicolas is able to be a part of AVI, we wil be there...
"Per Prosensa, the PRO051 trials will be conducted by GSK - timeline - JULY, AUGUST OR September 2010"
Just curious, I've heard 2 different things, are they still only testing exon 51 or going on at the same time starting others? I know they have 53 ready and it is one of top 4 to be done (according to reports). We need 53. Michelle
Just curious, I've heard 2 different things, are they still only testing exon 51 or going on at the same time starting others? I know they have 53 ready and it is one of top 4 to be done (according to reports). We need 53. Michelle
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