PPMD Community

Phil's Discussions (16)

View

Discussions Replied To (15)	Replies	Latest Activity
"Thanks Brian, I've read extensively about 'exon skipping' because it relates more…" Phil replied Dec 8, 2014 to Translarna	6	Dec 10, 2014 Reply by wainaina muiruri
"Could someone please point out to me a quick explanation between a nonsense mutation…" Phil replied Dec 4, 2014 to Translarna	6	Dec 10, 2014 Reply by wainaina muiruri
"Thanks Steven" Phil replied May 21, 2014 to No News About SMT C 1100!!!!!!!!!!!!	41	May 21, 2014 Reply by Michelle Scaglione
" "Another interesting side point is that they have lots of the drug already manufac…" Phil replied May 21, 2014 to No News About SMT C 1100!!!!!!!!!!!!	41	May 21, 2014 Reply by Michelle Scaglione
"Thanks Keith & Jason. " Phil replied Mar 11, 2014 to Whitehouse petition: Urge the FDA to Say YES to Accelerated Approval for children with Duchenne.	54	May 7, 2014 Reply by micro kid
"Hi Richard, my son Max has exon 43 deletion. Am I right in thinking exon 44 skipped…" Phil replied Mar 11, 2014 to Whitehouse petition: Urge the FDA to Say YES to Accelerated Approval for children with Duchenne.	54	May 7, 2014 Reply by micro kid
"I'm also concerned about accelerating the disease with respect to the heart.. but th…" Phil replied Mar 5, 2014 to Tadalafil phase 3 trial Eli Lilly & Co.	19	Nov 19, 2015 Reply by Rahul Deshpande
""The basis for the this trial was a similar one done with beckers, results showed th…" Phil replied Mar 4, 2014 to Tadalafil phase 3 trial Eli Lilly & Co.	19	Nov 19, 2015 Reply by Rahul Deshpande
""..this info sounds so good its almost unbelievable.." That's what went through my…" Phil replied Jun 5, 2013 to Genetic Editing Shows Promise in DMD	21	Jun 20, 2013 Reply by alfredo baccaglini
"I am also waiting. My son has exon 43 deletion. " Phil replied Apr 4, 2013 to Exon 44 skip	4	Apr 4, 2013 Reply by Jacobs Mommom