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New CRISPR-EXON SKIP technique could treat DMD https://www.sciencedaily.com/releases/2018/08/180816153147.htm "By editing a single base in genomic DNA using CRISPR-SKIP, we can eliminate… Started by Jason Darienzo	0	Aug 17, 2018
Muscular dystrophy patients could someday also benefit from this hydrogel successfully tested in mice https://www.sciencedaily.com/releases/2018/08/180815154502.htm Muscles of the elderly and of patients with Duchene muscular dystrophy have… Started by Jason Darienzo	0	Aug 17, 2018
Heat therapy boosts mitochondrial function in muscles Could help with hand function?. PPMD should look at this. Heat therapy boosts mitochondrial function in muscles Started by Jason Darienzo	0	Jul 31, 2018
Summit Announces PhaseOut DMD Did Not Meet Primary Endpoint Summit Announces PhaseOut DMD Did Not Meet Primary EndpointEzutromid Development to be DiscontinuedSummit to Focus on Advancing its Pipelin… Started by Jason Darienzo	1	Jul 11, 2018 Reply by Jason Darienzo
Steriod use at a later age? Hello, My son just turned 14 yrs old and was diagnosed with DMD at age 3. At the time of his diagnosis both his doctor and us agreed not to… Started by Rahel kebede	0	Jun 20, 2018
Utrophin Does anyone know if Summit is planning on conducting a Phase 3 trial after the Phase 2 trial is successful and we get positive results in t… Started by Sampreet	1	May 31, 2018 Reply by Aleksandar
Exon 52 deleted What medication do you use. Exondys 51? Started by Apple	0	May 26, 2018
Cholesterol Hi Have any of your boys experienced higher cholesterol and if so, have they been given statins or any other medication to address this? Started by Marks33	0	Apr 27, 2018
New CRISPR method efficiently corrects Duchenne muscular dystrophy defect in heart tissue Scientists have developed a CRISPR gene-editing technique that can potentially correct a majority of the 3,000 mutations that cause Duchenn… Started by Jason Darienzo	1	Feb 7, 2018 Reply by Galia Ben Ishay
low back pain does anyone here know what should i do with my kid as he suffers from chronic low back pain. i mean is there any treatment that we should d… Started by ahmed Sayed Abdel Gawad	1	Feb 5, 2018 Reply by Kathi Kinnett