Research (1,240)

Discussions Replies Latest Activity


Does anyone know if Summit is planning on conducting a Phase 3 trial after the Phase 2 trial is successful and we get positive results in t…

Started by Sampreet

1 May 31, 2018
Reply by Aleksandar

Exon 52 deleted

What medication do you use. Exondys 51?

Started by Apple

0 May 26, 2018


Hi Have any of your boys experienced higher cholesterol and if so, have they been given statins or any other medication to address this? 

Started by Marks33

0 Apr 27, 2018

New CRISPR method efficiently corrects Duchenne muscular dystrophy defect in heart tissue

Scientists have developed a CRISPR gene-editing technique that can potentially correct a majority of the 3,000 mutations that cause Duchenn…

Started by Jason Darienzo

1 Feb 7, 2018
Reply by Galia Ben Ishay

low back pain

does anyone here know what should i do with my kid as he suffers from chronic low back pain. i mean is there any treatment that we should d…

Started by ahmed Sayed Abdel Gawad

1 Feb 5, 2018
Reply by Kathi Kinnett

‘muscle memory’ exists at a DNA level Are there any implications on periodic dosing of steroid for DMD? 

Started by Jason Darienzo

0 Jan 30, 2018


Anyone giving Idebenone to your kids?If so, what dose and is it having anche impact?

Started by Michele Di Iorio

0 Jan 26, 2018

Facebook DMD Groups

Five months ago I found this forum and hoped that it would be a source of information about Duchenne.  Unfortunately I found that participa…

Started by Bruce Ward

0 Jan 21, 2018

Tamoxifen clinical trials

Good day, Does anyone knows if tamoxifen is recruiting now as I read before that the estimated enrollment date will be on September 2017,an…

Started by Shady

11 Jan 21, 2018
Reply by Sandro


Dear all, My 9 years old son has been taking Tamoxifen for 2 months now. He is taken care of by a wonderful team in Hadassah Hospital, Jeru…

Started by Galia Ben Ishay

47 Jan 21, 2018
Reply by Sandro


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