Research (1,240)

Discussions Replies Latest Activity

Utrophin

Does anyone know if Summit is planning on conducting a Phase 3 trial after the Phase 2 trial is successful and we get positive results in t…

Started by Sampreet

1 May 31, 2018
Reply by Aleksandar

Exon 52 deleted

What medication do you use. Exondys 51?

Started by Apple

0 May 26, 2018

Cholesterol

Hi Have any of your boys experienced higher cholesterol and if so, have they been given statins or any other medication to address this? 

Started by Marks33

0 Apr 27, 2018

New CRISPR method efficiently corrects Duchenne muscular dystrophy defect in heart tissue

Scientists have developed a CRISPR gene-editing technique that can potentially correct a majority of the 3,000 mutations that cause Duchenn…

Started by Jason Darienzo

1 Feb 7, 2018
Reply by Galia Ben Ishay

low back pain

does anyone here know what should i do with my kid as he suffers from chronic low back pain. i mean is there any treatment that we should d…

Started by ahmed Sayed Abdel Gawad

1 Feb 5, 2018
Reply by Kathi Kinnett

‘muscle memory’ exists at a DNA level

https://www.sciencedaily.com/releases/2018/01/180130091144.htm Are there any implications on periodic dosing of steroid for DMD? 

Started by Jason Darienzo

0 Jan 30, 2018

IDEBENONE

Anyone giving Idebenone to your kids?If so, what dose and is it having anche impact?

Started by Michele Di Iorio

0 Jan 26, 2018

Facebook DMD Groups

Five months ago I found this forum and hoped that it would be a source of information about Duchenne.  Unfortunately I found that participa…

Started by Bruce Ward

0 Jan 21, 2018

Tamoxifen clinical trials

Good day, Does anyone knows if tamoxifen is recruiting now as I read before that the estimated enrollment date will be on September 2017,an…

Started by Shady

11 Jan 21, 2018
Reply by Sandro

Tamoxifen

Dear all, My 9 years old son has been taking Tamoxifen for 2 months now. He is taken care of by a wonderful team in Hadassah Hospital, Jeru…

Started by Galia Ben Ishay

47 Jan 21, 2018
Reply by Sandro

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