Research (1,218)

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Propose research that is important to you Adding your experiences with Duchenne or Becker to ongoing research is vital to improve care and optimize potential therapies. But our com… Started by Holly PeayLatest Reply
Staff If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be? If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be? PPMD’s 2012 Co… Started by Kathi KinnettLatest Reply
Heart Transplant update We wanted to give a update on Josh. Joshs 3yr. Heart Transplant anniversary is March 24!!! Transplant CAN be done in DMD!!!! Josh is prepar… Started by TammyLatest Reply

Featured Discussions

Propose research that is important to you

Adding your experiences with Duchenne or Becker to ongoing research is vital to improve care and optimize potential therapies. But our com…

Started by Holly PeayLatest Reply

Staff

If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be?

If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be? PPMD’s 2012 Co…

Started by Kathi KinnettLatest Reply

Heart Transplant update

We wanted to give a update on Josh. Joshs 3yr. Heart Transplant anniversary is March 24!!! Transplant CAN be done in DMD!!!! Josh is prepar…

Started by TammyLatest Reply

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Discussions	Replies	Latest Activity
'CRISPR-Gold' fixes Duchenne muscular dystrophy mutation in mice without viral vector Scientists at the University of California, Berkeley, have engineered a new way to deliver CRISPR-Cas9 gene-editing technology inside cells… Started by Jason Darienzo	4	Oct 15 Reply by Jason Darienzo
crispr-Dr Eric olsan Hi Yesterday I Watched a video.Dr olson told crispr. summary deletıon of exon: use to crispr and dmd convert to becker( ıts look like ex… Started by ulas demirci	1	Oct 4 Reply by Bruce Ward
crispr-Dr Eric olsan Hi Yesterday I Watched a video.Dr olson told crispr. summary deletıon of exon: use to crispr and dmd convert to becker( ıts look like ex… Started by ulas demirci	0	Oct 4
Tamoxifen Dear all, My 9 years old son has been taking Tamoxifen for 2 months now. He is taken care of by a wonderful team in Hadassah Hospital, Jeru… Started by Galia Ben Ishay	45	Sep 30 Reply by Bruce Ward
Tamoxifen clinical trials Good day, Does anyone knows if tamoxifen is recruiting now as I read before that the estimated enrollment date will be on September 2017,an… Started by Shady	8	Sep 29 Reply by Alex
Exon 45 skipping/ exon 51 skipping, Help to make a hard decision !!.PLEASE HELP. Hi We are planning to participate in exon 45 skipping trail, for our 12 year old son. Is any one already enrolled in the exon skipping tr… Started by sulthana shaik	8	Sep 25 Reply by Kirubha Balakumar
idebenone Are You giving idebenone to your kids?does it really help?does anyone uses it instead of steroids? Started by Michele Di Iorio	1	Sep 25 Reply by Bruce Ward
Exon 17 Duplication Hi my son has duplication (Exon 17) anybody with that specific Exon 17 duplication? Started by ruben lengler	1	Sep 22 Reply by David
Ataluren Today I received a letter from California children services denying services for my son because he is in the trial Ataluren , they said he… Started by Azucena Lopez de Nava	3	Sep 18 Reply by Antonio Castro
Exon Duplications Hi All, Clinical research is going on Deletions. Anybody has any idea on Duplication's research. Serepta Pharma working on 40-53 Deletions.… Started by Sai Chand. Gurujala	0	Sep 11