Research (1,245)

Featured Discussions

Propose research that is important to you

Adding your experiences with Duchenne or Becker to ongoing research is vital to improve care and optimize potential therapies. But our com…

Started by Holly PeayLatest Reply


Staff

If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be?

If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be? PPMD’s 2012 Co…

Started by Kathi KinnettLatest Reply

Heart Transplant update

We wanted to give a update on Josh. Joshs 3yr. Heart Transplant anniversary is March 24!!! Transplant CAN be done in DMD!!!! Josh is prepar…

Started by TammyLatest Reply

Discussions Replies Latest Activity

Duchanee muscular dystrophy and heart transplant

https://gofund.me/492af803

Started by Paras Patel

1 Jul 23
Reply by Paras Patel

Muscle twitches/body spasms

Anyone else with DMD experiencing whole body muscle twitching/spasms that are uncontrollable?  Our son has had them and very scary because…

Started by Theresa Blake

0 Jul 20

Deflazacort versus Prednisone

Hi, my 5 year old son was recently diagnosed with Duchenne. We are due to start him on Deflazacort next week. We also have the option of gi…

Started by Tania

0 May 10

Non-Contiguous Mutations

I know this may be a long shot but does anyone have a non-contiguous duplication mutation? Our son has a duplication at 8-18 then again at…

Started by Ashlie Robinson

0 Feb 19

3yr old looking for suggestions

My son is 3 we live in an area with little to no services, he seems sore sometimes and his doctor thought maybe you guys would have ideas?

Started by Jennifer

1 Jan 20
Reply by Nicole Herring

Success Stories for exon 52 drug

Has there been any studies on how the exon 52 approved drug is doing? I believe it has been on the market for 3 years .

Started by william flannery

0 Mar 12, 2020

Latest Webinar on Gene therapy

Is this webinar available for review

Started by william flannery

2 Mar 12, 2020
Reply by william flannery

Manifesting carriers

My son and I have deletion of 10-16. I am symptomatic. Not sure what to do. I have always been very active. After my son was born I started…

Started by Lori

1 Jan 29, 2020
Reply by Karen Gabel

entering the toilet

greetings my son now suffers when he wants to go to the toilet when he is in school. is there any ideas about facilitating this issue for h…

Started by ahmed Sayed Abdel Gawad

1 Feb 13, 2019
Reply by Melissa Chamness

Exon 44 n 45 deletion

https://musculardystrophynews.com/2018/11/15/cureduchenne-avidity-hosting-webinar-potential-dmd-therapies/

Started by Shelly

0 Nov 20, 2018

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