May 2014
PTC gets EU approval
<a href="http://ir.ptcbio.com/ReleaseDetail.cfm?ReleaseID=850246">http://ir.ptcbio.com/ReleaseDetail.cfm?ReleaseID=850246</a>
PTC THERAPEUTICS RECEIVES POSITIVE OPINION FROM CHMP FOR TRANSLARNA™ (ATALUREN)
- The first treatment for the underlying cause of Duchenne mus…
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PTC gets EU approval
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February 2013
Another Muscular Dystrophy Mystery Solved; S…
Duchenne muscular dystrophy (DMD), predominantly affecting males, is the most common type of muscular dystrophy. Patients with Duchenne muscular dystrophy have a gene mutation that disrupts the produ…
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Another Muscular Dystrophy Mystery Solved; S…
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January 2013
Webinar: Ataluren Update with PTC
video
Webinar: Ataluren Update with PTC
3 Favorites
Webinar: Ataluren Update with PTC
event
Webinar: Ataluren Update with PTC
7 Favorites
December 2012
Good oral health reduces the risk of muscle…
This work, published in 2011, has been the scientific article about sports most consulted in the rank established by the BioMedLib Journal.
Maintaining a proper oral health is essential to prev…
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Good oral health reduces the risk of muscle…
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Webinar: Cardiac Interventions
video
Webinar: Cardiac Interventions
1 Favorite
June 2012
My Voice: Elizabeth Heller, 25 years old
Elizabeth Heller, is a woman living a full life – student, activist, wife –…
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My Voice: Elizabeth Heller, 25 years old
2 Favorites
PPMD Leads Critical Letter for Rare Disease C
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PPMD Leads Critical Letter for Rare Disease C
4 Favorites
February 2012
Matt
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Matt
1 Favorite
PPMD FDA Policy and PDUFA
I don’t know about you, but when I am in DC or receive government related information, I am always about 3 acronyms behind in the conversation. PDUFA – this is one acronym you want to…
Blog
PPMD FDA Policy and PDUFA
1 Favorite
January 2012
trapped
I am not sure how long we sat there together. Me trapped underneath my eighteen year old Cody. His immobile body laid across my…
Blog
trapped
2 Favorites
December 2011
Tivorsan Pharmaceuticals Biglycan: DMD resea…
<a href="http://www.pbn.com/detail.html?sub_id=bbe3d8f0d64a&page=1">http://www.pbn.com/detail.html?sub_id=bbe3d8f0d64a&page=1</a>
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Tivorsan Pharmaceuticals Biglycan: DMD resea…
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My Greatest Wish
I posted this on Facebook but felt I should share this here also. I have 3 wonderful boys. Tom is 16, Kevin is 13 and Brian is 10. Tom and Kevin have DMD, Brian does not.
I…
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My Greatest Wish
3 Favorites
PPMD’s 2011 Report Card
This time of year everyone is in holiday mode, or getting into holiday…
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PPMD’s 2011 Report Card
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October 2011
September 2011
NORD Submits Citizen's Petition to FDA Regard
I am proud to have joined the NORD board earlier this year. And I am particularly proud of the petition recently submitted to the FDA.
NORD's petition raises the collective voice…
Blog
NORD Submits Citizen's Petition to FDA Regard
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Leveraging the United Way: Raise money to fig
The annual, Fall United Way campaigns are getting underway throughout the country. Last year many…
Blog
Leveraging the United Way: Raise money to fig
3 Favorites
Word Association
9.24.11
This month is our month. As a community, September has come to mean the start of the school year, vacations are over, sleeves are rolled…
Blog
Word Association
3 Favorites
August 2011
Johnny and Julie’s X-Cellent Wedding
Next to Jenny and Kris’ wedding, this wedding of Johnny and Julie was perfect in every way. It was X-cellent because it was held at Xavier University, Bellarmine Chapel. Johnny had called me…
Blog
Johnny and Julie’s X-Cellent Wedding
9 Favorites
Homemade Tater Tot
I have a blog that you are all welcome to read - www.homemadetatertot.blogspot.com It is also featured on the Washington University Center for…
Blog
Homemade Tater Tot
1 Favorite
Heart Failure Drugs Preserve Muscle in Muscu…
What about this, any comments?
Both of them are apporoved drugs, farmacological approach and near treatment?
Am I missing something or this could be very promissing ...at least?
http://medicalcente…
Discussion
Heart Failure Drugs Preserve Muscle in Muscu…
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