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Blazena Kaderabkova's Favorites

May 2014

PTC gets EU approval <a href="http://ir.ptcbio.com/ReleaseDetail.cfm?ReleaseID=850246">http://ir.ptcbio.com/ReleaseDetail.cfm?ReleaseID=850246</a> PTC THERAPEUTICS RECEIVES POSITIVE OPINION FROM CHMP FOR TRANSLARNA™ (ATALUREN) - The first treatment for the underlying cause of Duchenne mus… Discussion PTC gets EU approval 2 Favorites

February 2013

Another Muscular Dystrophy Mystery Solved; S… Duchenne muscular dystrophy (DMD), predominantly affecting males, is the most common type of muscular dystrophy. Patients with Duchenne muscular dystrophy have a gene mutation that disrupts the produ… Discussion Another Muscular Dystrophy Mystery Solved; S… 1 Favorite

January 2013

Webinar: Ataluren Update with PTC

video Webinar: Ataluren Update with PTC 3 Favorites Webinar: Ataluren Update with PTC

event Webinar: Ataluren Update with PTC 7 Favorites

December 2012

Good oral health reduces the risk of muscle… This work, published in 2011, has been the scientific article about sports most consulted in the rank established by the BioMedLib Journal. Maintaining a proper oral health is essential to prev… Discussion Good oral health reduces the risk of muscle… 1 Favorite Webinar: Cardiac Interventions

video Webinar: Cardiac Interventions 1 Favorite

June 2012

My Voice: Elizabeth Heller, 25 years old

Elizabeth Heller, is a woman living a full life – student, activist, wife –…

Blog My Voice: Elizabeth Heller, 25 years old 2 Favorites PPMD Leads Critical Letter for Rare Disease C

Blog PPMD Leads Critical Letter for Rare Disease C 4 Favorites

February 2012

Matt

photo Matt 1 Favorite PPMD FDA Policy and PDUFA

I don’t know about you, but when I am in DC or receive government related information, I am always about 3 acronyms behind in the conversation. PDUFA – this is one acronym you want to…

Blog PPMD FDA Policy and PDUFA 1 Favorite

January 2012

trapped

I am not sure how long we sat there together. Me trapped underneath my eighteen year old Cody. His immobile body laid across my…

Blog trapped 2 Favorites

December 2011

Tivorsan Pharmaceuticals Biglycan: DMD resea… <a href="http://www.pbn.com/detail.html?sub_id=bbe3d8f0d64a&page=1">http://www.pbn.com/detail.html?sub_id=bbe3d8f0d64a&page=1</a> Discussion Tivorsan Pharmaceuticals Biglycan: DMD resea… 1 Favorite My Greatest Wish

I posted this on Facebook but felt I should share this here also. I have 3 wonderful boys. Tom is 16, Kevin is 13 and Brian is 10. Tom and Kevin have DMD, Brian does not.

I…

Blog My Greatest Wish 3 Favorites PPMD’s 2011 Report Card

This time of year everyone is in holiday mode, or getting into holiday…

Blog PPMD’s 2011 Report Card 1 Favorite

October 2011

September 2011

NORD Submits Citizen's Petition to FDA Regard

I am proud to have joined the NORD board earlier this year. And I am particularly proud of the petition recently submitted to the FDA.

NORD's petition raises the collective voice…

Blog NORD Submits Citizen's Petition to FDA Regard 1 Favorite Leveraging the United Way: Raise money to fig

The annual, Fall United Way campaigns are getting underway throughout the country. Last year many…

Blog Leveraging the United Way: Raise money to fig 3 Favorites Word Association

9.24.11

This month is our month. As a community, September has come to mean the start of the school year, vacations are over, sleeves are rolled…

Blog Word Association 3 Favorites

August 2011

Johnny and Julie’s X-Cellent Wedding

Next to Jenny and Kris’ wedding, this wedding of Johnny and Julie was perfect in every way. It was X-cellent because it was held at Xavier University, Bellarmine Chapel. Johnny had called me…

Blog Johnny and Julie’s X-Cellent Wedding 9 Favorites Homemade Tater Tot I have a blog that you are all welcome to read - www.homemadetatertot.blogspot.com It is also featured on the Washington University Center for… Blog Homemade Tater Tot 1 Favorite Heart Failure Drugs Preserve Muscle in Muscu… What about this, any comments? Both of them are apporoved drugs, farmacological approach and near treatment? Am I missing something or this could be very promissing ...at least? http://medicalcente… Discussion Heart Failure Drugs Preserve Muscle in Muscu… 1 Favorite