We are excited to welcome the two newest members of our Scientific Advisory Committee, Dongsheng Duan, PhD and Jill Rafael-Fortney, PhD! Our Scientific Advisory Committee, chaired by PPMD Senior Scientific Advisor Dr. Lee Sweeney, includes leading experts in basic and clinical Duchenne research and Duchenne clinical management. The committee expertly reviews every grant that comes in and offers funding or advice on how to proceed to garner funding in the future.
Thank you Drs. Duan and Rafael-Fortney for lending your expertise to our mission to end Duchenne!
Dr. Duan received his Ph.D. from the University of Pennsylvania in 1997 and is the recipient of a number of honors and awards, including: 2004 Spurgeon Distinguished Medical Research Award, University of Missouri; 2006 Outstanding New Investigator Award, American Society of Gene Therapy; 2008 Margaret Proctor Mulligan Professor, University of Missouri; 2009 Chancellor’s Award for Outstanding Research and Creative Activity, University of Missouri and 2010- Member, Muscular Dystrophy Association Scientific Advisory Committee.
Duan worked as a research associate at the Chinese Academy of Medical Sciences and as a post-doc and visiting assistant professor at the University of Iowa.
Areas of Research Interest include: Adeno-associated Virus (AAV) transduction biology; AAV gene therapy for Duchenne muscular dystrophy; Cardiomyopathy in Duchenne muscular dystrophy; Dystrophin biology Canine model of muscular dystrophy; NOS signaling and nitrosative stress in skeletal muscle and Free radical Injury in muscle aging and muscular dystrophy.
The overall goal of her laboratory is to identify novel treatment strategies for both skeletal muscles and the heart in Duchenne muscular dystrophy patients. Her lab uses mouse models to unravel the molecular pathogenesis of Duchenne, identify novel molecular treatment targets, and test potential therapeutic approaches.
She was the recipient of a prestigious Burroughs Wellcome Fund Career Award and an American Heart Association Established Investigator Award. Her research is currently supported by the NIH and DOD, and has also been supported the Muscular Dystrophy Association, Parent Project Muscular Dystrophy, and CureDuchenne.
She has published over 50 papers on muscular dystrophy and cardiomyopathy in peer-reviewed journals. In addition, she has supported the development of many young scientists and has participated in a variety of advocacy and outreach activities to convey the importance of biomedical research.
Dr. Fortney received her B.A. from Cornell University, her Ph.D. from the Department of Human Genetics at the University of Michigan, and carried out her postdoctoral training at the University of Oxford, England.
PPMD's Scientific Advisory Committee
View our full Scientific Advisory Committee at ParentProjectMD.org/SAC