Parent Project Muscular Dystrophy believes in the promise that gene therapy holds for the Duchenne community. And so we set an ambitious fundraising goal for our Gene Therapy Initiative. In fact, $500,000 is our largest fundraising goal ever.
And once again, you—our incredibly dedicated community—really came through. You not only matched but exceeded our goal! You never cease to amaze me, and I’m so overwhelmed by your commitment and your courage.
Your gifts will push forward vital work in gene therapy at different levels of development—from deepening our investments in microdystrophin and CRISPR, to exploring newer gene therapies like GALGT2 and Dup2.
I’m so grateful for the continued commitment of the community and I am inspired by your courage. You helped us close out 2017 on such a positive note (a year that could really use some good news!) and kick-start the new year as passionate as ever to tackle our mission.
We will not rest until every person affected by Duchenne can turn to a life-saving treatment. Thank you for joining the fight to end Duchenne.
Here’s to a happy and healthy 2018!