I lost my beautiful son to Duchenne, four years ago. My son was stolen from me, and the same disease that claimed his life, continues to claim so many more children's lives.DMD is 100% fatal, no doubt about it, we will continue to loose children until someone stops this killer. Approve the use of Eteplirsen, please, what if it was your boy? This drug is helping twelve boys and has had no side effects. We have nothing to loose only to gain. My son Nicholas is in heaven and I will see him again someday, therefore I continue to live, but this was not available for my Nick, please save as many lives as you can, by approving this drug.
This killer disease needs to be stopped! Like my precious Nick, these boys deserve to live free from Duchenne.