This time of year, all of us at Parent Project Muscular Dystrophy like to take a moment to look back, reflect, and give thanks. And as a member of our inner circle, you’re vital to our work.
I’m thankful to you, for the part you play in our vibrant PPMD community, and for taking such an active role in our accomplishments this year:
Research — We’ve seen promising therapies make it further into the clinical trials pipeline, including Duchenne’s first-ever Phase 2b clinical trial with PTC 124 and the first trials in Exon Skipping
. We’re thankful to our relentless, brilliant researchers for getting us ever closer to the day we end Duchenne.
Advocacy — In this heated election year, we weren’t sure if our Advocacy efforts were going to prevail. When President Bush signed the renewal of the MD-Care Act
into law, it was a day for the entire muscular dystrophy community to celebrate. We’re thankful to our many tireless advocates, who worked so hard to make sure our voice wasn’t lost in the halls of Congress.
Community — Despite tough economic times and high gas prices over the summer, our annual conference was the biggest yet. We’re thankful to the researchers, physicians, and other presenters, as well as the PPMD families for their participation in this event. We are also thankful for all of your support for the Run For Our Sons teams, the Coach to Cure MD
campaign and all of the local events that demonstrate our unity and passion.
Education — We are grateful for the outreach and education that DuchenneConnect
has provided for the worldwide Duchenne population. We are also thankful to the Centers for Disease Control and Prevention, with whom we collaborated to educate families and healthcare professionals. This year alone more than a 1,000 families reached out to us because of our education efforts. We’re thankful to our many partners that help raise awareness around the country.
As I look back at these accomplishments, I am struck by how thankful I am that the Duchenne community is one that’s passionate about affecting change. You are a community that gets things done.
And I would love to hear what you’re thankful for. Please take a moment to share your favorite accomplishments from this past year and who or what you have to thank for them
Happy Thanksgiving from our family to yours!