Help us raise $250,000 by 12/31!
I’m just a few weeks shy of my first-year anniversary working at Parent Project Muscular Dystrophy—and what a year it’s been! I fell in love with the passion and determination of this community years ago through my career in pediatric health, and it has been incredible to be in the trenches with you all.
Now we are moving toward a new year following our first FDA approval—and with promising therapies like CRISPR/Cas9 entering our research pipeline. Never has there been so much potential.
Last week, Dr. Eric Olson gave a special webinar for our community about his lab’s cutting-edge work with CRISPR/Cas9. Now we are ready to see what it can do for people living with Duchenne.
As with any new technology there are still many questions that must be answered about CRISPR/Cas9 before we can understand just how much it can do to end Duchenne. How stable is this dystrophin protein produced by CRISPR/Cas9? What are the safety risks?
As a mom, I would do anything for my son to help him live the life he dreams—and I know that every mother and father in this community wants the same. While I can’t truly know how it feels to have a child with Duchenne, the urgency and passion you feel every day is clear in each conversation I’ve had with families like yours.
It is your stories—of hope, successes, and struggles—that inspire me to do everything I can to help end Duchenne. Please make a donation to PPMD today—a donation that will be matched dollar for dollar to help us find out just how much CRISPR/Cas9 can do!
Your gift helps us invest in research strategies like CRISPR/Cas9 that have the potential to help every single family in our community.
Thank you for your belief in PPMD and happy holidays from my family to yours!
Senior Vice President of Research Strategy
Parent Project Muscular Dystrophy