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Regardless of what you celebrate this time of year (if anything) or whether the holiday season brings out a sense of wonder and magic, or not…I think we all have a little part of us that still hopes for miracles, especially in December. Twinkly lights, beautifully wrapped presents, roaring fires, delicious food. This is the time of year when, if a miracle is going to happen, it seems like it should go ahead and happen.

The fight to end Duchenne doesn’t need miracles or magic though. There are so many talented people – in science, research, care, industry, regulatory, government – spending day after day making the impossible, possible. I’ve written about the strides in Duchenne many times, but it’s true. While nothing will be fast enough for our sons and daughters living with Duchenne, I hope there is some comfort in knowing that progress is happening and at a rate unlike any other time in Duchenne’s history.

When I look at the continued updates from industry (as you’ll read below in our Research Section), or that we are going to reauthorize the MD-CARE Act for a second time (with your help!), or attend a gala with a wonderful group of generous people new to our community (read Mary-Lou’s blog), or meet a young man who inspires and educates (have you met Mohammed Haider yet?) – I believe what was impossible years ago, will be possible in the near future.

On behalf of myself and your dedicated, passionate family at PPMD, have a wonderful holiday season and a joyous 2013 – and thank you, for being the miracle in my life. Together we can make the impossible, possible. Together, we can end Duchenne.

 

Where we are & what we're doing

PPMD makes it a priority to attend the most important meetings and conferences related to Duchenne, as well as connecting with the leaders in the field to move research, care, and advocacy forward.


See where we’ve been and where we are going:

  • 12/6: PPMD's first EndDuchenne Gala
  • 12/7-9: Kathi attends the ENMC workshop on Exon Skipping
  • 12/15: Pat and Ryan attend the FACES Northern NY launch
  • 12/17-18: Pat, Sharon, and Ryan host industry meetings
  • 1/15: RFOS at Walt Disney World Marathon Weekend
  • 1/16: Sharon attends Orphan Drug Meeting
  • 1/16: PPMD hosts webinar with PTC

 

 




Pat Furlong, Founding President, CEO
Read more PPMD Staff Blogs


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