The study of previously treated boys nmBMD/DMD with Ataluren was prolonged for the next one year, see http://clinicaltrials.gov/ct2/show/NCT01247207?term=ataluren&ra...

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Comment by Miguel Vte. López Rodríguez on November 2, 2011 at 7:38pm

What are waiting the EMEA (European Medical Agency) to aprove the phase III trial in Europe and the FDA or EMEA to aprove the orphan drug!!!

Comment by Blazena Kaderabkova on August 22, 2011 at 9:36am
We hoped that PTC will try to get approval already this year.
Comment by Clare Harper on August 22, 2011 at 8:21am

This drug obviously helps somewhat,think ptc needs to consider another trial with new boys in addition to the current extension,to create access for those boys that may benefit...

 

Comment by Blazena Kaderabkova on August 22, 2011 at 8:05am
I dont know. We were surprised. May be some update from PTC will explain it.
Comment by Clare Harper on August 22, 2011 at 7:25am
i wish PTC would communicate regular updates to the community,it is so hard to find out where they feel they are at,
Comment by Tracey Hartz on August 20, 2011 at 4:41pm
so does this mean they will not be going for FDA approval this year, like we all hoped?

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