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83 International Experts Submit Letter to FDA Encouraging Approval of Ataluren

PPMD applauds the group of 83 international experts with experience caring for Duchenne patients around the globe who have written a letter to the FDA encouraging approval of ataluren. With hundreds of patients accessing ataluren through the conditional approval by EMA, these physicians have first-hand experience observing the impact of the drug in a real-world setting. We will continue to work on behalf of the Duchenne community towards U.S. access and approval of ataluren for every single one.

Click here to view the letter.

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