Hallo, I just joined this PPMD Community and send regards to all participants. Many of you will know me because I am writing reports on the many research approaches for a therapy of Duchenne dystrophy.
Thank you, Pat, for your so immediate messages from this very important exon-skipping conference in Cold Spring Harbor. In this context, everybody might be interested to see the interview which I recorded with Gerard Platenburg at the PPMD meeting in Philadelphia last July. Gerard explains details about the completed first "local" exon-skipping trial and also about the second, the "systemic", trial which is now being performed. Those who have not seen this interview yet, should send me their e-mail address, and they will get it as pdf file. The interview exists also in German and Spanish. I also have an interview about PTC124, recorded at the PTC company in South Plainfield, NJ, on 21 July.
Guenter Scheuerbrandt, PhD.
(still in Cadaqués in Spain at the moment, and in the Black Forest in Germany during the winter)
20 October 2008