PPMD's Blog – October 2017 Archive (7)

Letter from PTC Therapeutics to the Community Following FDA Decision

PTC has shared a letter with the Duchenne community in regards to the recent FDA decision. PTC will be holding a community call on Friday, October 27 at 12:00 PM EST to discuss next steps with the community. Please e-mail your…

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Added by PPMD on October 26, 2017 at 9:30am — No Comments

News from 2017 World Muscle Society: Part 2

Annie Kennedy and Kathi Kinnett from the PPMD team recently attended the 22nd International Annual Congress of the World Muscle Society and have been reporting back the latest updates related to…

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Added by PPMD on October 9, 2017 at 12:30pm — No Comments

83 International Experts Submit Letter to FDA Encouraging Approval of Ataluren

PPMD applauds the group of 83 international experts with experience caring for Duchenne patients around the globe who have written a letter to the FDA encouraging approval of ataluren. With hundreds of patients accessing ataluren through the…

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Added by PPMD on October 9, 2017 at 10:36am — No Comments

News from 2017 World Muscle Society: Part 1

 

Annie Kennedy and Kathi Kinnett from the PPMD team are attending the 22nd International Annual Congress of the World Muscle Society and will be reporting back over the next couple of days. More…

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Added by PPMD on October 6, 2017 at 1:30pm — No Comments

Catabasis Reports Positive Results from Open-Label Extension of MoveDMD Trial with Edasalonexent

Catabasis Pharmaceuticals, Inc. today reported new positive efficacy results following 24 and 36 weeks of treatment with 100 mg/kg/day oral edasalonexent in the MoveDMD Phase 2 trial open-label…

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Added by PPMD on October 4, 2017 at 10:30am — 1 Comment

Letter from PTC Therapeutics to the Community Following FDA Ad Comm

PTC Therapeutics President and CEO, Stuart Peltz, Ph.D has shared a letter with the Duchenne community following last week's Advisory Committee Meeting at…

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Added by PPMD on October 3, 2017 at 9:30am — No Comments

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