With so many exciting happenings at PPMD and in our community, it is too easy to rush from one “fire” to the next and forget to celebrate our successes. Take a moment with us, and check out one success: our new Care for Duchenne pages.
We created the new…Continue
Results to Be Submitted to FDA with a Goal of Accelerating Review of Duchenne Therapies
PPMD has conducted a rigorous survey of more than 100 parents whose children have Duchenne, gathering invaluable perspectives as to treatment priorities and risk threshold based on realistic but hypothetical treatments - information that PPMD is encouraging regulators to use to accelerate review time and, ultimately, to speed access to…Continue
Added by PPMD on June 11, 2013 at 2:00pm — No Comments
Added by PPMD on June 7, 2013 at 8:30am — No Comments