PPMD's Blog – March 2016 Archive (7)

Summit Reports Positive Interim Data from New Formulation of SMT C1100 in Duchenne

Summit Therapeutics announced positive interim data from a Phase 1 clinical trial evaluating a new oral formulation of its lead utrophin modulator, SMT C1100, for Duchenne. In this dose escalating clinical trial's…

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Added by PPMD on March 30, 2016 at 9:30am — No Comments

ReveraGen BioPharma Receives $3M for Phase 2 Studies of Vamorolone in Duchenne

PPMD is thrilled to see the continued progress of VBP-15, now known as Vamorolone. Progress to date includes a first in-human study of healthy volunteers and animal data which suggests it has none of the side effects of steroids, does not impact linear growth, and does not promote…

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Added by PPMD on March 28, 2016 at 2:30pm — 1 Comment

How You Can Participate in the Eteplirsen Ad Comm

The Duchenne community is working closely together to prepare for the April 25 Advisory Committee Meeting for Sarepta’s therapy eteplirsen. PPMD, the Duchenne Alliance, the Center for DMD at UCLA, Jett Foundation, and the Race to Yes…

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Added by PPMD on March 15, 2016 at 9:00am — No Comments

FDA Releases New Date for Eteplirsen Ad Comm

At long last we have received information regarding the rescheduled Advisory Committee for Sarepta (eteplirsen). The Ad Comm will take place on Monday, April 25 at the College Park Marriott Hotel & Conference Center (a non-FDA campus…

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Added by PPMD on March 10, 2016 at 9:00am — No Comments

How You Can Participate in Upcoming FDA Advisory Committee Meetings

UPCOMING AD COMMS

Sarepta…

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Added by PPMD on March 10, 2016 at 9:00am — No Comments

PPMD Launches the Every Single [One] Tour

For 22 years, PPMD has brought together families with leading experts, care providers, and industry partners through our Annual Connect Conference, FACES…

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Added by PPMD on March 4, 2016 at 10:00am — 1 Comment

Registration for PPMD's 2016 Connect Conference is Now Open

Parent Project Muscular Dystrophy's Annual Connect Conference is a unique convergence of industry partners, scientific leaders, medical providers, people living with Duchenne, and their families. This exceptional meeting has grown to…

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Added by PPMD on March 1, 2016 at 9:30am — No Comments

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