Yesterday, Kymriah, a gene therapy made by Novartis that treats an aggressive type of leukemia was approved for children and young adults. The new commissioner of the FDA, Dr. Scott Gottlieb, remarked on the FDA's approval of the first gene…Continue
Added by Abby Bronson on August 31, 2017 at 1:00pm — No Comments
With trials in gene therapy on the horizon, and terms like "cassette", "construct", "promoter", and "transduce" being thrown around, we want to ensure that you, our Duchenne Community, has all the knowledge you need to navigate the world of gene therapy.
Earlier this month, PPMD hosted a webinar with Lee Sweeney, PhD (University…
Added by Abby Bronson on August 23, 2017 at 8:00pm — No Comments