Abby Bronson's Blog – March 2016 Archive (3)

Update on Gene Replacement/Repair Strategies for Duchenne Muscular Dystrophy

There has been a flurry of press recently on gene therapy in Duchenne muscular dystrophy and CRISPR technology. With this barrage of information, PPMD wanted to take a deeper dive into gene therapy as a potential treatment for Duchenne.


An Expert Opinion…


Added by Abby Bronson on March 25, 2016 at 9:30am — No Comments

PPMD is Initial Partner in OnPAR — Online Partnership to Accelerate Research

The National Institutes of Health (NIH) is one of the biggest funders of medical research in the US, and projects it has funded have touched almost every Duchenne therapeutic in development now in some way. In FY2016, the NIH is investing nearly $32.3 billion in medical research, and of…


Added by Abby Bronson on March 24, 2016 at 9:30am — No Comments

Gene Therapy Today: Notes from PPMD’s Duchenne Gene Therapy Forum

Gene therapy.

Those two words have been tossed around for some time, starting in the late 1990s when several gene therapy trials started, but ended with fatal results. Now, when the field has learned a lot from those initial results and with optimized technologies, we come back to gene therapy as a viable option for genetic diseases. This renewed…


Added by Abby Bronson on March 8, 2016 at 12:00pm — 4 Comments

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