We are all acutely aware of the need for an effective treatment for Duchenne. Finding a way for children and young men affected by Duchenne to lead longer, healthier lives is at the heart of all of our efforts as families’ fight this devastating disease.
This week PPMD received an…
ContinueAdded by Sharon Hesterlee on August 31, 2012 at 10:30am — 2 Comments
One approach to improving muscle strength in Duchenne is to replace unhealthy muscle cells that lack dystrophin with donor stem cells that have normal levels of dystrophin. These cells might come from a relative unaffected by Duchenne or even a person with Duchenne’s own cell, after dystrophin is restored though a technique like gene therapy.
Although we’ve…
ContinueAdded by Sharon Hesterlee on August 29, 2012 at 2:00pm — 6 Comments
As Sarepta (formely AVI) announces promising results from its phase II interim data and GSK follows up its promising phase…
Added by Sharon Hesterlee on August 8, 2012 at 8:30pm — 14 Comments
© 2021 Created by PPMD.
Powered by
Badges | Report an Issue | Privacy Policy | Terms of Service