PPMD Community

All Blog Posts Tagged 'Staff' (372)


Staff
Parent Project Muscular Dystrophy Awards UCLA $50,000 Exploratory Grant for Evaluation of Exon Skipping Enhancers in Duchenne

PPMD announced today that they will award Dr. M. Carrie Miceli and her team at UCLA’s David Geffen School of Medicine and College of Letters and Science, a $50,000 exploratory grant to continue their evaluation of exon skipping boosters for the treatment of Duchenne. 

 

Duchenne muscular…

Continue

Added by PPMD on January 29, 2015 at 1:00pm — 1 Comment


Staff
Get Active in Advocacy

2014 was a historic year in our community. 2015 promises to be another critical year in Duchenne and we need you to help keep the momentum going! Just look at the ‘to-do’ list:



  • MD-Care Act amendment implementation begins
  • New Drug Applications submissions expected by several companies
  • The FDA has stated publicly…
Continue

Added by Ryan Fischer on January 28, 2015 at 1:30pm — No Comments


Staff
FDA Acknowledges the Importance of Benefit-Risk Preferences: Why this Matters to Duchenne

This started as a blog about the second publication on PPMD’s benefit/risk study, which was published in late December in a journal called The Patient (and more on that later). But something remarkable happened this week that helps frame…

Continue

Added by Holly Peay on January 26, 2015 at 10:23am — No Comments


Staff
Important Vaccinations Recommendations

Vaccinations are very, very important to protect us against infection and disease – but they are also very, very confusing. 

Some vaccines are “live,” some are “attenuated (killed),” some protect against…

Continue

Added by Kathi Kinnett on January 23, 2015 at 12:00pm — No Comments


Staff
BMS & The Voice of the Patient

For the last two years, global biopharmaceutical company Bristol-Myers Squibb (BMS) has organized a day when all of their drug development project teams from across the world would have the opportunity to take some time to…

Continue

Added by Pat Furlong on January 22, 2015 at 10:30am — 1 Comment


Staff
Meet our 2015 PPMD Adult Advisory Council!

“We were the generation that was hoped for… And now we’re here.” L. Vance Taylor

The PPMD Adult Advisory Council (PAAC) serves to ensure that the voices of adults living with Duchenne and Becker…

Continue

Added by Annie Kennedy on January 15, 2015 at 1:00pm — No Comments


Staff
PPMD Welcomes New CEO, John Porter, PhD

We're excited to announce that John Porter, PhD, former program director of the National Institutes of Health (NIH)/National Institute of Neurological Disorders and Stroke (NINDS) will take on the role of Chief Executive Officer for Parent Project Muscular…

Continue

Added by PPMD on January 12, 2015 at 9:00am — No Comments


Staff
Without Endings There Are No Beginnings…

It’s New Year’s Day 2015 and I think Janus, the two-headed Roman God who looks forward and backwards at the same time, is a fitting representation of my life right now. I need to tell you all that I have had to make a difficult decision this year—at the end of this month I will…

Continue

Added by Sharon Hesterlee on January 5, 2015 at 1:30pm — 1 Comment


Staff
Nearly there!

We’re so close. Thanks to the strength and generosity of this incredible community, we are only $36,200 from our goal of $400,000 to fund combination therapies. There’s still time for you to help us reach our goal.…

Continue

Added by Pat Furlong on December 31, 2014 at 8:51am — No Comments


Staff
Heart Failure Drugs Slow Deadly Damage in Duchenne, Offering New Hope

In a new study led by Dr. Subha Raman of The Ohio State University Wexner Medical Center, researchers were able to dramatically slow the rate of heart damage in patients with Duchenne muscular dystrophy by using a combination of well-established drugs.…

Continue

Added by Kathi Kinnett on December 29, 2014 at 7:00pm — 1 Comment


Staff
Now is the time for strength.

We’ve been working toward this moment for years. And the time for action is now.



When I started with PPMD in 2009, Pat Furlong and I talked a lot about what it would take to end Duchenne. We knew it wouldn’t be one thing, and we knew it wouldn’t be easy. We believed that only a combination of therapies could address the entire disease within the body.…



Continue

Added by Sharon Hesterlee on December 18, 2014 at 3:02pm — No Comments


Staff
The Solid Suit: Combining Forces to Enhance Strength

(Pictured from left to right: Stanley Nelson, MD, Center for Duchenne Muscular Dystrophy at UCLA, Thomas Sugar, PhD, Arizona State University Polytechnic School, Tom Egan, SRI International, Roy…

Continue

Added by Annie Kennedy on December 18, 2014 at 9:57am — No Comments


Staff
Pfizer Initiates Phase 2 Study of PF-06252616 in Duchenne Muscular Dystrophy

Pfizer Inc. announced today enrollment of the first patient in a multicenter Phase II clinical trial of the investigational compound PF-06252616 in boys with Duchenne muscular dystrophy (DMD), a genetic disorder characterized by progressive muscle degeneration and weakness. PF-06252616 is an experimental, infused,…

Continue

Added by PPMD on December 17, 2014 at 9:00am — No Comments


Staff
PPMD Names Massachusetts General Hospital a Certified Duchenne Care Center

Today Parent Project Muscular Dystrophy (PPMD) named Massachusetts General Hospital (MGH) our sixth Certified Duchenne Care Center, recognizing the Hospital’s dedication to improving care…

Continue

Added by PPMD on December 16, 2014 at 2:03pm — 2 Comments


Staff
PPMD Holds Congressional Briefing

It was seven months to the day that Representatives Upton and DeGette first launched this bold initiative called 21st Century Cures. In fact, that hearing that would set in motion months and months of proposals for sweeping changes to research infrastructure and academic systems took place…

Continue

Added by Annie Kennedy on December 16, 2014 at 9:30am — No Comments


Staff
Ventilation FAQ Booklet from the DMD Pathfinders

If you were able to listen to the third recording of the pulmonary webinar series (Adult Duchenne Pulmonary Care), you heard Dr. Sheehan mention the publication of a new booklet,…

Continue

Added by Kathi Kinnett on December 15, 2014 at 11:28am — No Comments


Staff
PPMD To Collaborate With Catabasis Pharmaceuticals, Inc. On CAT-1004 Development

Parent Project Muscular Dystrophy (PPMD) announced today a collaboration with Catabasis Pharmaceuticals, Inc. (Catabasis) to assist in a Phase 2 clinical trial of its CAT-1004 product candidate for the treatment of patients with Duchenne. As part of this…

Continue

Added by PPMD on December 11, 2014 at 11:23am — No Comments


Staff
PPMD Calls for Greater Transparency and Accountability of FDA Patient Engagement Efforts

Parent Project Muscular Dystrophy (PPMD) is urging Congress to build upon gains in recent years to further strengthen and enhance programs to ensure the patient voice is heeded during the drug development process during a…

Continue

Added by Ryan Fischer on December 8, 2014 at 1:30pm — No Comments


Staff
Parent Project Muscular Dystrophy Awards Akashi Therapeutics, Inc. $500,000 Grant

Parent Project Muscular Dystrophy (PPMD) has awarded Akashi Therapeutics, Inc. (Akashi) a $500,000 grant to fund clinical trials to test the safety and efficacy of an…

Continue

Added by PPMD on December 8, 2014 at 10:36am — No Comments


Staff
ABLE Act Changes Disability Landscape – This just got real!

If you’re like many families, birthdays and holidays often bring gifts from friends and loved ones far and wide. As my son just celebrated his fourth birthday, he would tear through packages in the hope of finding a new Lego set or Ninja Turtle. He was a bit less interested in the envelopes that accompanied the gifts but patiently waited as Mommy read the cards to him and announced who each gift was from. And the concept of monetary gifts was a bit lost on him. The…

Continue

Added by Annie Kennedy on December 3, 2014 at 6:00pm — No Comments

Monthly Archives

2015

2014

2013

2012

2011

2010

2009

2008

2007

© 2015   Created by PPMD.

Badges  |  Report an Issue  |  Privacy Policy  |  Terms of Service