Dr. Ryszard Kole from AVI Biopharma and PPMD President Pat Furlong further reflect on recent findings that Duchenne is a stem cell disease. Read the discussion below, as well as, Pat’s previous blog.

I read with interest your blog yesterday regarding the Cell paper on Duchenne that came out on Monday. I can very well understand the excitement, as well as some possible confusion, that the paper generated among PPMD…

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The Google Alerts were flying last week with Helen Blau’s recent paper about the new mouse model for Duchenne muscular dystrophy that implicates stem cells. The Facebook messages suggested this was something new, some new news. Actually, this is not new. The only thing new is this new mouse model.



The loss of satellite cells in Duchenne is well documented. In early discussions…

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Washington, DC.



The news from Washington, DC is constant with multiple agendas and many moving parts. Following the November elections of 2010, we have many new faces in both the House and Senate. The ripple effect of the elections is that committees will change, priorities will change, and many, many may not be familiar with Duchenne muscular dystrophy.



This year marks 10 years of advocating for Duchenne muscular dystrophy and…

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Experts in the field of endocrinology, neurology, pediatrics, and rehabilitative medicine met at Kennedy Kreiger to discuss endocrine issues in Duchenne. Alan Rogol, M.D., Ph.D. chaired the first session. In the endocrine community, Alan is considered one of the world’s best. The meeting included 40 individuals representing endocrinology, neurology, cardiology, rheumatology, rehabilitation, and orthopedics. Craig McDonald discussed the effect of steroid on the natural history of Duchenne.… Continue