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Featured Blog Posts – October 2015 Archive (4)

Staff PPMD Submits Results of Patient-Centered Benefit-Risk Assessment Study in Duchenne & Becker to FDA

PPMD is pleased to announce that late yesterday we submitted the results of our most recent patient-centered benefit-risk assessment (PCBR) study to the FDA. The assessment was done with research partners at the Johns Hopkins Bloomberg School of Public Health. PCBR assessment is an increasingly-favored…

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Added by PPMD on October 22, 2015 at 7:48am — No Comments

Staff Ad Comms Update: Group Letter Submitted to FDA

PPMD is proud to help author and share the attached letter to Dr. Janet Woodcock, Director of the Center for Drug Evaluation and Research at the FDA. Along with CDMD at…

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Added by PPMD on October 19, 2015 at 11:00am — No Comments

Staff Ad Comms Update: An Overwhelming Day

Today we learned that the FDA will host an Advisory Committee (Ad Comm) meeting on November 24 to discuss the NDA for BioMarin’s drisapersen…

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Added by Pat Furlong on October 14, 2015 at 4:30pm — No Comments

Staff PPMD Urges Senate to Move Forward on #Cures2015 Innovation for Healthier Americans Bill

Yesterday, I had the distinct privilege of representing PPMD and our Duchenne community as I sat before a full room of Senate staffers and congressional aides in the Dirksen Senate office building. Our goal was to urge them to press forward on the Innovation for Healthier Americans bill (also referred to as the ‘Innovation…

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Added by Annie Kennedy on October 9, 2015 at 12:00pm — 1 Comment