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Featured Blog Posts – May 2014 Archive (3)

Staff Congressional Committee That Funds the FDA Recognizes PPMD-Led Efforts on Benefit/Risk, Draft Guidance; Applauds Collaboration with Agency

For the first time ever, the appropriations bill that funds the Food and Drug Administration includes report language focused on Duchenne muscular dystrophy and championed by PPMD advocates.

This week the House Appropriations Committee approved the Fiscal Year 2015 Department of Agriculture and FDA…

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Added by Pat Furlong on May 30, 2014 at 11:22am — No Comments

Staff A Good Day for Duchenne

EMA grants Conditional Approval for Ataluren

Ataluren, PTC Therapeutics’ nonsense suppression drug received Conditional…

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Added by Pat Furlong on May 23, 2014 at 9:30am — 6 Comments

Staff PPMD Congressional Champions Voice the Need for Action on the MD-CARE Act

On May 20th, the House Energy and Commerce Subcommittee on Health held a hearing entitled, 21st Century Cures: The President’s Council of Advisors on Science and Technology (PCAST) Report on Drug Innovation.

The hearing was led by Chairman Joe Pitts (R-PA) and is part of the new 21st Century Cures initiative that seeks to accelerate the discovery, development and delivery of promising new treatments to patients.…

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Added by Ryan Fischer on May 22, 2014 at 3:30pm — No Comments