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Parent Project Muscular Dystrophy (PPMD)

Profile Information

About me:
Parent Project Muscular Dystrophy’s mission is to end Duchenne. We accelerate research, raise our voices in Washington, demand optimal care for all young men, and educate the global community.

email: Community@ParentProjectMD.org
phone: 800-714-5437
City:
Hackensack, NJ

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PPMD's Blog

Summit to Extend Ongoing PhaseOut DMD Clinical Trial of Ezutromid in Patients with Duchenne Muscular Dystrophy

Posted on March 27, 2017 at 11:25am 0 Comments

Summit Therapeutics announced today that it will proceed with the planned extension phase of PhaseOut DMD, a Phase 2 clinical trial evaluating the utrophin modulator ezutromid, subject to regulatory approval.



This follows an interim review of the safety and tolerability data from the ongoing trial by an independent Data…

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Latest Activity


Staff
PPMD posted blog posts
14 hours ago

Staff
PPMD posted blog posts
Friday
Lisa Hied Dilworth is attending PPMD's event
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[Upcoming Webinar] Akashi Provides Update on HT-100 at Online Webinar - Eastern Time Zone

March 27, 2017 from 1:30pm to 2:30pm
Monday, March 27 at 1:30 PM ESTPlease join Parent Project Muscular Dystrophy and Akashi Therapeutics as we host a webinar Monday, March 27 at 1:30 PM ET to discuss HT-100 and next steps for the clinical program.Akashi CEO Marc Blaustein will present data from the previous clinical program of HT-100 and discuss FDA’s recent decision to allow the clinical development of HT-100 to resume, and leave time for discussion and fielding of questions.Speakers:Pat FurlongFounding President & CEO,…See More
Thursday

Staff
PPMD posted an event
Thumbnail

[Upcoming Webinar] Akashi Provides Update on HT-100 at Online Webinar - Eastern Time Zone

March 27, 2017 from 1:30pm to 2:30pm
Monday, March 27 at 1:30 PM ESTPlease join Parent Project Muscular Dystrophy and Akashi Therapeutics as we host a webinar Monday, March 27 at 1:30 PM ET to discuss HT-100 and next steps for the clinical program.Akashi CEO Marc Blaustein will present data from the previous clinical program of HT-100 and discuss FDA’s recent decision to allow the clinical development of HT-100 to resume, and leave time for discussion and fielding of questions.Speakers:Pat FurlongFounding President & CEO,…See More
Thursday

Staff
PPMD posted a blog post

Akashi Therapeutics Receives FDA Clearance to Resume HT-100 Clinical Development

PPMD is pleased to learn that the FDA has completed its review and concluded that Akashi Therapeutics may resume clinical development of HT-100 (delayed-release halofuginone) in people with Duchenne (click here to read Akashi's press release). Preventing fibrosis is an important target and an essential piece of a combination of therapies that will be…See More
Wednesday

Staff
PPMD posted a blog post
Mar 16
T. Wright joined PPMD's group
Mar 12
Rahul Deshpande joined PPMD's group
Mar 9

Comment Wall (19 comments)

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At 6:15am on October 24, 2015, Anca Felicia Lutas said…

Thank you! he always smiles!

At 9:42pm on October 23, 2015, Anca Felicia Lutas said…
Thank you very much!
He always smiles!
At 7:34am on February 18, 2015, Subodh Joshi said…

great effort. is there any thought of initiating this work in india?

i am a 50 years old patient. still working in disability area. much scope for such work here.

At 5:49am on October 16, 2014, Hassan K. Shehu Shehu said…
I lost two of my three children with duchenne dmd,the last one has started to show signs of gowers. He only takes prediniselone for almost six months now ,please help me with advice .
At 5:45pm on March 1, 2012, LYNN JONES said…

I'm sorry if i upset anyone with my message of any families with young boys, we experienced the most wonderful, fulfilling,caring, happy, joyous i could go on and on..of our lives with our darling boy he brought us so much pleasure we miss him so much but we will go on and carry on raising awareness and raising funds for the hospice (derian house) they were a fantastic support and still are   enjoy everyday and live for every moment xxx

At 5:39pm on March 1, 2012, LYNN JONES said…

Thank you for replying to my message, its been the hardest few months of our lives, matthew was our world and we miss him like i cant explain, he was loved so much by all his family. he was such a well and happy boy, his passing came as such a shock it was so sudden and unexpected, we had had such a perfect day with him i still cant believe it happened and how we are coping without him with us.  you read literature regarding the boys condition and me and my husband believed we were so lucky with matthew as he had always been in such good health, we were so lucky. when the boys reach a certain age things change for them and we didnt see it coming (something i will never forgive myself for) the care matthew received once in adult services wasnt the same or as through. thank you once again for replying its good to type away my thoughts xxx love lynn

At 5:32pm on February 22, 2012, cercel alexandra silvia said…

thank you verry much!

At 11:41am on October 27, 2011, Damien Howey said…

thank u and i was wondering how we can get stuff going in North Dakota

At 11:37am on October 24, 2011, Anca Felicia Lutas said…

Thank you!

At 10:35pm on October 7, 2011, Mrs. Joseph Wood said…
Thank you so much! We are hoping to connect with others that are successfully finding ways to improve the quality of life for their sons.. and working to find a cure! I would be blessed by the information you mentioned. I'll take a look at that link. Thank you again for the welcome!
 
 
 

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