Kevin Freel
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  • Dallas, TX
  • United States
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Kevin Freel's Discussions

NICE Recommends Translarna

Started this discussion. Last reply by Shelly Apr 16, 2016. 5 Replies

Positive news for Translarna today.http://ir.ptcbio.com/releasedetail.cfm?ReleaseID=965331Continue

 

Kevin Freel's Page

Latest Activity

David favorited Kevin Freel's discussion NICE Recommends Translarna
Apr 17, 2016
Shelly favorited Kevin Freel's discussion NICE Recommends Translarna
Apr 16, 2016
Shelly replied to Kevin Freel's discussion NICE Recommends Translarna
"Great news!!!!"
Apr 16, 2016
Nida Zuberi favorited Kevin Freel's discussion NICE Recommends Translarna
Apr 15, 2016
Nida Zuberi favorited Kevin Freel's discussion NICE Recommends Translarna
Apr 15, 2016
Nida Zuberi replied to Kevin Freel's discussion NICE Recommends Translarna
"This may help push FDA to reconsider. PTC is now resubmitting their file to the Canadian health organization too. Let's see if they approve it. Is there anything we can do to push for a FDA approval. Isn't time of the essence here."
Apr 15, 2016
Jay Griffin favorited Kevin Freel's discussion NICE Recommends Translarna
Apr 15, 2016
Aleksandar replied to Kevin Freel's discussion NICE Recommends Translarna
"Translarna is for nonsense mutation. This approval is even more frustrating to US citizens. Nice always seemed stricter as far as New Drugs are approved then rest of the world, yet they approve Translarna, but FDA does not even warrant a review.…"
Apr 15, 2016
Jay Griffin replied to Kevin Freel's discussion NICE Recommends Translarna
"If I am not mistaken, it's exon 51... This could not be shipped to the US.. My son deletions 51-55 (not eligible even it was approved in the US. I am very happy for them. This approval gives great momentum for the DMD community around the world"
Apr 15, 2016
Keith & Jill VE replied to Kevin Freel's discussion NICE Recommends Translarna
"This is great news!   Forgive my ignorance, but would this help boys without a nonsense mutation, deletions for example?  Also, any possibility to have the product shipped to the US, like deflazacort?"
Apr 15, 2016
Kevin Freel posted a discussion
Apr 15, 2016
Kevin Freel is now a member of PPMD Community
Mar 30, 2016

Profile Information

Name(s) of child(ren)/individual(s) with Duchenne:
Jackson
Age(s) of child(ren)/individual(s) with Duchenne:
0-3
City:
Dallas
State:
TX

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