PTC124 Phase 2a Extension Study Families

24 members Latest Activity: Jan 19, 2016 This group is intended to be for families of the 38 boys who participated in the clinical trial of PTC124 phase 2a, to be able to share with each…

PTC 124-2b Clinical Trial

31 members Latest Activity: May 1, 2018 Various issues re: PTC 124 Clinical Trials for current or prospective participants worldwide

Adolescence (age 7-12)

120 members Latest Activity: Oct 13, 2021

Duchenne Parents

247 members Latest Activity: Nov 20, 2019

Cincinnati Children's Hospital Medical Center

193 members Latest Activity: Sep 17, 2015

For families who take their children to Cincinnati Children's Hospital for DMD/BMD  medical care.

Michigan Families

42 members Latest Activity: Dec 27, 2015 MD families living in the State of Michigan