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Patient Specific Exon Skipping -NOW!

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Pushing forward a venture that will concentrate on that.

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31 members Latest Activity: May 1, 2018 Various issues re: PTC 124 Clinical Trials for current or prospective participants worldwide

Duchenne Smiles

115 members Latest Activity: Feb 27, 2014 A Duchenne smile is a True smile, cannot be faked and exemplifies true enjoyment.