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Premature Stop Codon Discussions (12)

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Discussions	Replies	Latest Activity
Can someone who's boy is getting Ataluren / PTC124 speak to the benefits? Hi, I am eager for information from any / all parents who's boys have been part of the Ataluren trials. Can you speak to your perception… Started by John Smith	3	Jan 26, 2012 Reply by John Smith
Any word on potential FDA approval date for Ataluren / PTC 124 ? Hello, Anybody out there? Was wondering if anyone had any word on a possible Ataluren / PTC 124 approval time frame. Or, if anyone has… Started by John Smith	1	Sep 2, 2011 Reply by Chad Studebaker
Ataluren - PTC124 Bob, Jacob was on the drug high dose for over a year. We felt like he had more mobility and energy when taking the drug. Not sure if thi… Started by Chad Studebaker	3	Dec 13, 2010 Reply by John Smith
Vision problems? Has anyone's son had vision problems that came to light from a yearly school check? Depth, ocular motor, etc.?We've noticed he has a diffi… Started by Michelle	0	Feb 8, 2010
PTC124 and steroids Hi there, I was just wondering if any of the boys enrolled in the current Phase 2b trial are not taking steroids - and whether any of the… Started by Marks33	1	Jul 1, 2009 Reply by Perlita & Gordy Hains
Tried to enroll our son into the PTC124/2b trial - no luck so far - so frustrated Hi all My name is Berit from Norway, and we have a 9 year old boy with a "nonsense" mutation. He fits ALL the inclusion criteria to partic… Started by BeritSofie	2	Nov 29, 2008 Reply by BeritSofie
124b extension details? We are currently considering whether to enrol our son in the PTC124b clinical trial. He was not in the phase 2a. Does anyone know (based o… Started by brad stringer	3	Oct 17, 2008 Reply by brad stringer
Gentamacin Hi there, I note from the Clinical Trials website there is a 6 month phase 1 trial for DMD with stop codons, currently recruiting, for Gen… Started by Marks33	1	Sep 7, 2008 Reply by Tammy Gregory
Recent PTC Litigation In case you have not seen the article, be aware that a parent of a stop-codon child has filed suit against PTC Theraputics. Obviously we ar… Started by Michelle	1	Aug 21, 2008 Reply by Tamara Walters
PTC124 upcoming Trial and its requirements... My son turns 5 in October and we hope to have him screened as a possible participant for the PTC124 study here at CHoP at that time. My wif… Started by Paul Johnson	7	Aug 21, 2008 Reply by Tamara Walters