Has anyone heard anything about Utrophin trials and what is happening with that.
I feel like the Duchenne world is moving forward which I am so happy for but what about the boys with in-frame deletions. Exon skipping will not work, PTC124 will not work, when are we going to get some good news for our boys as well. I get happy when I read about exon skipping and PTC but get upset for my nephew because not one of these breakthru's can help him.

Views: 59

Replies to This Discussion

There was some discussion on the main board in the research forum about a month ago.

http://community.parentprojectmd.org/forum/topics/updates-about-summit

Basically, the trial that Biomarin was going to do this year has been delayed.

RSS

Need help using this community site? Visit Ning's Help Page.

Members

Events

© 2018   Created by PPMD.   Powered by

Badges  |  Report an Issue  |  Privacy Policy  |  Terms of Service