It seems almost 10% of DMD cases are due to deletion of exon 44. But the trials for exon skipping for 44 deletion is still in very early phase. Anyone having update on this.
Sarepta is working on an exon skip of 45 and I believe they stated in a call that they hoped to start trials late this year.
pls advise whether exon skip of 45 is for duchene delete 46-50 ?