It seems almost 10% of DMD cases are due to deletion of exon 44. But the trials for exon skipping for 44 deletion is still in very early phase. Anyone having update on this.

 

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Sarepta is working on an exon skip of 45 and I believe they stated in a call that they hoped to start trials late this year.

Hello

pls advise whether exon skip of 45 is for duchene delete 46-50 ?

thanks 

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