Research presentations at the Connect Conference
We are just putting the final touches on the agenda for both the Connect Conference and the first annual DMD Therapeutic Development conference. Both conferences will take place in parallel in Denver this summer (June 24-26).
The research conference will feature technical presentations focused on DMD therapy development and is intended primarily for the scientific audience, but those registered for the Connect Conference are welcome to attend any scientific session as observers. The main clinical trial updates session will actually be a joint session of scientists and familes and includes the following talks (all presenters confirmed):
Saturday, June 26th
7:00-8:00am Breakfast—clinical research from the company perspective (GSK)
8:20-12pm Clinical Trials Update (Joint Session with families) (Chair: Kevin Flanigan)
8:30-8:40am Intro to Clinical Trials, Kevin Flanigan, Nationwide Children’s Research Institute
8:40-9:00am Utrophin upregulator, Saba Sile, Biomarin
9:00-9:20am Ataluren update, Leone Atkinson, PTC Therapeutics
9:20-9:40am Exon-skipping, AVI-4658, Steven Shrewsbury , AVI Biopharma
9:40-10:00am Exon-skipping, GKS 2402968, John Kraus, GSK
10:00-10:20am Sildenafil, Kathryn Wagner, Kennedy Krieger Research Institute
10:20-10:40am Q&A
10:40-10:50am BREAK
10:50-11:10am Lisinopril vs. Losartan, Jerry Mendell, Nationwide Children’s Research Institute
11:10-11:30am FOR-DMD (NIH Steroid trial), Kate Bushby, Newcastle University
11:30-11:50am ACE O31, Diana Escolar, Kennedy Krieger Research Institute
11:50-12:10am Follistatin gene therapy, Jerry Mendell, Nationwide Children’s Research Institute
12:10-12:30pm Q & A
You can find more information about the conference including agendas for both the Connect conference and the DMD Therapeutic Development Conference at http://www.parentprojectmd.org/site/PageServer?pagename=ending_atte....
Sharon
Replies to This Discussion
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Permalink Reply by Ofelia Marin on
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This looks great. So sorry I cannot attend.
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Permalink Reply by jenn on
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i too am wishing we could make it this year, the expense and time off, coupled with child care needs.....i cant wait to hear from those who are attending
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Permalink Reply by Sharon Hesterlee on
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As an update to my earlier posting about the conference, here are the abstracts for the DMD Therapeutic Development meeting--the scientific conference that will take place in parallel with the Annual Connect conference. Thought some of you who couldn't make the conference would still be interested... (see attachment)
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Permalink Reply by Melanie Sunny on
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Will the Clinical Trials Update at the Connect Conference be published in the PPMD website?
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We will post what we can--we may not be allowed to post some of the company presentations, but I'll see if we can at least do a summary that they will sign off on and let us post.
Melanie Sunny said:Will the Clinical Trials Update at the Connect Conference be published in the PPMD website?
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Sharon,
Thank you very much!
-Melanie
Sharon Hesterlee said:We will post what we can--we may not be allowed to post some of the company presentations, but I'll see if we can at least do a summary that they will sign off on and let us post.
Melanie Sunny said:Will the Clinical Trials Update at the Connect Conference be published in the PPMD website?
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How soon can they be posted?
Sharon Hesterlee said:We will post what we can--we may not be allowed to post some of the company presentations, but I'll see if we can at least do a summary that they will sign off on and let us post.
Melanie Sunny said:Will the Clinical Trials Update at the Connect Conference be published in the PPMD website?
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