We are just putting the final touches on the agenda for both the Connect Conference and the first annual DMD Therapeutic Development conference.   Both conferences will take place in parallel in Denver this summer (June 24-26). 

 

The research conference will feature technical presentations focused on DMD therapy development and is intended primarily for the scientific audience, but those registered for the Connect Conference are welcome to attend any scientific session as observers.  The main clinical trial updates session will actually be a joint session of scientists and familes and includes the following talks (all presenters confirmed):

 

Saturday, June 26th

 

7:00-8:00am                       Breakfast—clinical research from the company perspective (GSK)

 

8:20-12pm                           Clinical Trials Update (Joint Session with families) (Chair: Kevin Flanigan)

 

8:30-8:40am                       Intro to Clinical Trials, Kevin Flanigan, Nationwide Children’s Research Institute

 

8:40-9:00am                       Utrophin upregulator, Saba Sile, Biomarin

 

9:00-9:20am                       Ataluren update, Leone Atkinson, PTC Therapeutics

 

9:20-9:40am                       Exon-skipping, AVI-4658,  Steven Shrewsbury , AVI Biopharma

 

9:40-10:00am                     Exon-skipping, GKS 2402968, John Kraus, GSK

 

10:00-10:20am                   Sildenafil, Kathryn Wagner, Kennedy Krieger Research Institute

 

10:20-10:40am                   Q&A

 

10:40-10:50am                   BREAK

 

10:50-11:10am                   Lisinopril vs. Losartan, Jerry Mendell, Nationwide Children’s Research Institute

 

11:10-11:30am                   FOR-DMD (NIH Steroid trial), Kate Bushby, Newcastle University

 

11:30-11:50am                   ACE  O31, Diana Escolar, Kennedy Krieger Research Institute

 

11:50-12:10am                   Follistatin gene therapy, Jerry Mendell, Nationwide Children’s Research Institute

 

12:10-12:30pm                  Q & A

 

 

You can find more information about the conference including agendas for both the Connect conference and the DMD Therapeutic Development Conference at http://www.parentprojectmd.org/site/PageServer?pagename=ending_atte....

 

Sharon

 

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This looks great. So sorry I cannot attend.
i too am wishing we could make it this year, the expense and time off, coupled with child care needs.....i cant wait to hear from those who are attending
As an update to my earlier posting about the conference, here are the abstracts for the DMD Therapeutic Development meeting--the scientific conference that will take place in parallel with the Annual Connect conference. Thought some of you who couldn't make the conference would still be interested... (see attachment)
Attachments:
Will the Clinical Trials Update at the Connect Conference be published in the PPMD website?
We will post what we can--we may not be allowed to post some of the company presentations, but I'll see if we can at least do a summary that they will sign off on and let us post.

Melanie Sunny said:
Will the Clinical Trials Update at the Connect Conference be published in the PPMD website?
Sharon,
Thank you very much!
-Melanie

Sharon Hesterlee said:
We will post what we can--we may not be allowed to post some of the company presentations, but I'll see if we can at least do a summary that they will sign off on and let us post.

Melanie Sunny said:
Will the Clinical Trials Update at the Connect Conference be published in the PPMD website?
How soon can they be posted?

Sharon Hesterlee said:
We will post what we can--we may not be allowed to post some of the company presentations, but I'll see if we can at least do a summary that they will sign off on and let us post.

Melanie Sunny said:
Will the Clinical Trials Update at the Connect Conference be published in the PPMD website?

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