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I believe that skipping 51 can also work for a group with deletion of 52 (not all of the 52 group, but some of them)
In fairness to Charley's fund, they do invest in other potential treatments for Duchenne kids.
My concern is that I would imagine the FDA would want to see the best outcome from this drug after the first trial here in the states. So, you would want to put your best first one and/or first 2 foward. Dr. Ed Connor at CNMC has this exon skipping theory, "leave no Duchenne kid behind." Meaning, we have got to get this right the first time so hopefully the rest will come later at a quicker pace and perhaps even altogether so parents don't have to worry over if they are carrying the 'Golden Willie Wonka' exon skipping ticket or not.
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