please watch this video on a succefull story with dmd on stem cells thank you

Success in stem cells

http://www.youtube.com/watch?v=Jyt2LHayjcs

a doctor is willing to have another phase of a trial on stem cells he already had 4 cases in which the kids had normal dintrophyn levels

 

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When Noah was ~2 we visited with Baylor Medical doctors who were experimenting with bone marrow transplant (cell therapy). Ultimately we did not participate due to the risks involved (infection, rejection) and the limited efficacy of the treatment. The doctors in that 'trial' were very realistic and had a lot of data they presented to the potential patients.

In this case, there is no real data that I can find. There is no real indication that at this point after the treatments there has been any improvement. I would want to know that I am not putting my child in imminent danger and that there would be a real benefit before proceeding.

Some good resources I found:

http://www.treat-nmd.eu/patients/stemcells/stemcelltourism/
http://stemcells.nih.gov/info/health.asp
I also see that Geron Corp, which has received FDA approval for its stem cell research, is seeing some success. If anything, if we can find a treatment to improve heart muscle function then that is significant progress.

http://www.reuters.com/article/idUSSGE64C0LC20100513

Watching the video again also reminded me that one of the issues limiting the success of the other trials was systemic delivery - that local changes to the muscle (normal dystrophin levels) were seen at the injection site only. Hopefully this obstacle can be overcome.

Conrad Klahn said:
When Noah was ~2 we visited with Baylor Medical doctors who were experimenting with bone marrow transplant (cell therapy). Ultimately we did not participate due to the risks involved (infection, rejection) and the limited efficacy of the treatment. The doctors in that 'trial' were very realistic and had a lot of data they presented to the potential patients.

In this case, there is no real data that I can find. There is no real indication that at this point after the treatments there has been any improvement. I would want to know that I am not putting my child in imminent danger and that there would be a real benefit before proceeding.

Some good resources I found:

http://www.treat-nmd.eu/patients/stemcells/stemcelltourism/
http://stemcells.nih.gov/info/health.asp
Missing the point here in older lads, just replacing dystrophin won't help because of the necrosis already, you need to replace the whole lot. If its all about the science wheres the data?
Thank you all for the information.
About the necrosis does the stem cells have the capability to regenerate the muscle tissue. Like the mesnchymals. I was wondering if this is so.

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