Gene therapy treats all muscles in the body in muscular dystrophy dogs

Gene therapy treats all muscles in the body in muscular dystrophy dogs

http://www.sciencedaily.com/releases/2015/10/151022141722.htm

Safe and bodywide muscle transduction in young adult Duchenne muscular dystrophy dogs with adeno-associated virus

http://hmg.oxfordjournals.org/content/24/20/5880

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Thanks for sharing Jason. The question is: does it concern all mutations?

They are actually adding a new smaller version of the dystrophin gene, so it will be for all mutations.  

I agree this is the solution for all mutations a larger effect if the therapy is conducted before the already extensive damage to muscle, It would be good if we reached with the FDA to fast track this therapy is the solution for our children!

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