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I am not 100% sure but I think if Exon 68 was skiped it would work for 63-67 deletion.
Look at FAQ on Prosensa's site http://prosensa.eu/patients-family/duchenne-muscular-dystrophy/faq/...
Hopefull, when the first 2 or 3 of these Exon Skipping drugs are approved the FDA give all "single Exon skip drugs" a quicker approval.
Jason, thank you so much. I almost felt that the only hope was upregulation of uptrophin. After seeing the page you linked to the discussion I have come to realize that if 68 can be skipped and using upregulation of uptrophin my son my have a fighting chance. I felt weak hearted but your help strengthend my heart and therefore I in-turn can be stronger for my beautiful son whom I love most unconditionally.
Thanks
Tom Hilliker
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